Phase I/II Trial of Diaphragm Delivery of Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase (rAAV1-CMV-GAA) Gene Vector in Patients with Pompe Disease
Author:
Affiliation:
1. Departments of Pediatrics and Surgery, University of Florida, Gainesville, FL 32611.
Publisher
Mary Ann Liebert Inc
Subject
Genetics (clinical)
Link
http://www.liebertpub.com/doi/pdf/10.1089/humc.2014.2514
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5. ATS/ERS Statement on Respiratory Muscle Testing
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