Immortalized Skin Fibroblasts Expressing Conditional MyoD as a Renewable and Reliable Source of Converted Human Muscle Cells to Assess Therapeutic Strategies for Muscular Dystrophies: Validation of an Exon-Skipping Approach to Restore Dystrophin in Duchenne Muscular Dystrophy Cells-Reference-Cited by-同舟云学术

Immortalized Skin Fibroblasts Expressing Conditional MyoD as a Renewable and Reliable Source of Converted Human Muscle Cells to Assess Therapeutic Strategies for Muscular Dystrophies: Validation of an Exon-Skipping Approach to Restore Dystrophin in Duchenne Muscular Dystrophy Cells

Published:2009-07 Issue:7 Volume:20 Page:784-790
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Chaouch Soraya¹²³,Mouly Vincent¹²³,Goyenvalle Aurélie⁴,Vulin Adeline¹²³,Mamchaoui Kamel¹²³,Negroni Elisa¹²³,Di Santo James⁵,Butler-Browne Gillian¹²³,Torrente Yvan⁶,Garcia Luis¹²³,Furling Denis¹²³

Affiliation:

1. Université Pierre et Marie Curie-Paris 06, UMRS 974, Paris F-75013, France.

2. INSERM, U974, Institut de Myologie, Paris F-75013, France.

3. CNRS, UMR 7215, Institut de Myologie, Paris F-75013, France.

4. Department of Physiology, Anatomy, and Genetics, University of Oxford, OX1 3QX Oxford, United Kingdom.

5. Unité des Cytokines et Développement Lymphoide, Institut Pasteur, Paris F-75015, France.

6. Stem Cell Laboratory of the Centro Dino Ferrari, Department of Neurological Sciences, Fondazione IRCCS Policlinico of Milan, University of Milan, 20122 Milan, Italy.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2008.163

Reference18 articles.

1. Therapeutic antisense-induced exon skipping in cultured muscle cells from six different DMD patients

2. Impact on oxidative phosphorylation of immortalization with the telomerase gene

3. Efficient control of gene expression in the hematopoietic system using a single Tet-on inducible lentiviral vector

4. Restoration of Human Dystrophin Following Transplantation of Exon-Skipping-Engineered DMD Patient Stem Cells into Dystrophic Mice

5. Extension of Life-Span by Introduction of Telomerase into Normal Human Cells

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