1. Department of Developmental Biology, National Research Institute for Child Health and Development, Tokyo 157-8535, Japan.
2. Laboratory of Genetic Diagnosis and Gene Therapy, Department of Genetics, National Research Institute for Child Health and Development, Tokyo 157-8535, Japan.
3. Department of Pediatrics, Tokyo Metropolitan Higashiyamato Medical Center for the Severely Disabled Japan, Tokyo 207-0022, Japan.
4. Laboratory of Stem Cell Therapy, Institute of Medical Science of the University of Tokyo, Tokyo 108-8639, Japan.
5. Division of Genetic Therapeutics, Center for Molecular Medicine, Jichi Medical University, Shimotsuke, Tochigi 329-0498, Japan.
6. Department of Clinical Laboratory Medicine, National Center for Child Health and Development, Tokyo 157-8535, Japan.
7. National Research Institute for Child Health and Development, Tokyo 157-8535, Japan.