Prevention of Lethal Murine Hypophosphatasia by Neonatal Ex Vivo Gene Therapy Using Lentivirally Transduced Bone Marrow Cells-Reference-Cited by-同舟云学术

Prevention of Lethal Murine Hypophosphatasia by Neonatal Ex Vivo Gene Therapy Using Lentivirally Transduced Bone Marrow Cells

Published:2015-12 Issue:12 Volume:26 Page:801-812
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Iijima Osamu¹,Miyake Koichi¹,Watanabe Atsushi¹²,Miyake Noriko¹,Igarashi Tsutomu¹³,Kanokoda Chizu¹,Nakamura-Takahashi Aki¹,Kinoshita Hideaki⁴,Noguchi Taku⁵,Abe Shinichi⁵,Narisawa Sonoko⁶,Millán José Luis⁶,Okada Takashi¹,Shimada Takashi¹

Affiliation:

1. Division of Gene Therapy, Department of Biochemistry and Molecular Biology, Research Center for Advanced Medical Technology, Nippon Medical School, Tokyo, Japan.

2. Division of Clinical Genetics, Nippon Medical School Hospital, Tokyo, Japan.

3. Department of Ophthalmology, Nippon Medical School Hospital, Tokyo, Japan.

4. Department of Dental Materials Science, Tokyo Dental College, Tokyo, Japan.

5. Department of Anatomy, Tokyo Dental College, Tokyo, Japan.

6. Sanford Children's Health Research Center, Sanford-Burnham Medical Research Institute, La Jolla, California.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2015.078

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2. Physiological role of alkaline phosphatase explored in hypophosphatasia

3. The Role of Phosphatases in the Initiation of Skeletal Mineralization

4. Alkaline phosphatase: placental and tissue-nonspecific isoenzymes hydrolyze phosphoethanolamine, inorganic pyrophosphate, and pyridoxal 5'-phosphate. Substrate accumulation in carriers of hypophosphatasia corrects during pregnancy.

5. Alkaline phosphatase is an ectoenzyme that acts on micromolar concentrations of natural substrates at physiologic pH in human osteosarcoma (SAOS-2) cells

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