Progress on Gene Therapy, Cell Therapy, and Pharmacological Strategies Toward the Treatment of Oculopharyngeal Muscular Dystrophy-Reference-Cited by-同舟云学术

Progress on Gene Therapy, Cell Therapy, and Pharmacological Strategies Toward the Treatment of Oculopharyngeal Muscular Dystrophy

Published:2015-05 Issue:5 Volume:26 Page:286-292
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Harish Pradeep¹,Malerba Alberto¹,Dickson George¹,Bachtarzi Houria²

Affiliation:

1. School of Biological Sciences, Royal Holloway–University of London, Surrey, TW20 0EX, United Kingdom.

2. Brighton Centre for Regenerative Medicine, School of Pharmacy and Biomolecular Sciences, University of Brighton, Brighton, BN2 4GJ, United Kingdom.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2015.014

Reference65 articles.

1. Hereditary Disorders in Saguenay-Lac-St-Jean (Quebec, Canada)

2. Short GCG expansions in the PABP2 gene cause oculopharyngeal muscular dystrophy

3. Oculopharyngeal MD among Bukhara Jews is due to a founder (GCG)9 mutation in the PABP2 gene

4. Oculopharyngeal muscular dystrophy: Recent advances in the understanding of the molecular pathogenic mechanisms and treatment strategies

5. The Poly(A)-Binding Protein Nuclear 1 Suppresses Alternative Cleavage and Polyadenylation Sites

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