Gene Therapy for X-Linked Severe Combined Immunodeficiency: Where Do We Stand?

Author:

Cavazzana Marina1234,Six Emmanuelle234,Lagresle-Peyrou Chantal234,André-Schmutz Isabelle234,Hacein-Bey-Abina Salima1256

Affiliation:

1. Biotherapy Department, Necker Children's Hospital, Assistance Publique-Hôpitaux de Paris, Paris

2. Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Ouest, Assistance Publique-Hôpitaux de Paris, INSERM, Paris

3. Paris Descartes–Sorbonne Paris Cité University, Imagine Institute, Paris

4. INSERM UMR 1163, Laboratory of Human Lymphohematopoiesis, Paris

5. UTCBS CNRS 8258-INSERM U1022, Faculté des Sciences Pharmaceutiques et Biologiques, Université Paris Descartes, Paris

6. Immunology Laboratory, Groupe Hospitalier Universitaire Paris-Sud, AP-HP, Le-Kremlin-Bicêtre, France.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

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