Dosage Thresholds and Influence of Transgene Cassette in Adeno-Associated Virus–Related Toxicity-Reference-Cited by-同舟云学术

Dosage Thresholds and Influence of Transgene Cassette in Adeno-Associated Virus–Related Toxicity

Published:2018-11 Issue:11 Volume:29 Page:1235-1241
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Khabou Hanen¹,Cordeau Chloé¹,Pacot Laure¹,Fisson Sylvain²,Dalkara Deniz¹

Affiliation:

1. Sorbonne Universités, UPMC Univ Paris 06, INSERM, CNRS, Institut de la Vision, Paris, France; and Inserm UMR_S951, Univ Evry, Université Paris-Saclay, EPHE, Evry, France.

2. Généthon, Inserm UMR_S951, Univ Evry, Université Paris-Saclay, EPHE, Evry, France.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2018.144

Reference44 articles.

1. Taking Stock of Retinal Gene Therapy: Looking Back and Moving Forward

2. Adeno-Associated Virus RNAs Appear in a Temporal Order and Their Splicing Is Stimulated during Coinfection with Adenovirus

3. Cloning of adeno-associated virus into pBR322: rescue of intact virus from the recombinant plasmid in human cells.

4. Transduction of Dendritic Cells by DNA Viral Vectors Directs the Immune Response to Transgene Products in Muscle Fibers

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