Suppression of Somatic Expansion As a Novel Therapeutic Approach for Huntington Disease and Other Repeat Expansion Disorders-Reference-Cited by-同舟云学术

Suppression of Somatic Expansion As a Novel Therapeutic Approach for Huntington Disease and Other Repeat Expansion Disorders

Published:2022-04-01 Issue:2 Volume:1 Page:163-175
ISSN:2768-1572
Container-title:GEN Biotechnology
language:en
Short-container-title:GEN Biotechnology

Author:

Antonijevic Irina A.¹^ORCID,Bettencourt Brian R.¹,Bialek Peter¹,Ge Pei¹,Ding Shi-Ying¹,Lai George¹,Hedde Joseph¹,Asp Eva¹^ORCID,Seth Meetu¹,Marnellos George¹,Whartenby Katharine A.²,Monckton Darren G.³,Tabrizi Sarah J.⁴

Affiliation:

1. R&D, Triplet Therapeutics, Inc., Cambridge, Massachusetts, USA; UCL Queen Square Institute of Neurology, and Dementia Research Institute at UCL, London, United Kingdom.

2. Freelance Consultant, Science Writer, Baltimore, Maryland, USA; UCL Queen Square Institute of Neurology, and Dementia Research Institute at UCL, London, United Kingdom.

3. Institute of Molecular, Cell and Systems Biology, College of Medical, Veterinary and Life Sciences, University of Glasgow, Glasgow, United Kingdom; and UCL Queen Square Institute of Neurology, and Dementia Research Institute at UCL, London, United Kingdom.

4. Huntington's Disease Centre, UCL Queen Square Institute of Neurology, and Dementia Research Institute at UCL, London, United Kingdom.

Publisher

Mary Ann Liebert Inc

Link

https://www.liebertpub.com/doi/pdf/10.1089/genbio.2021.0012

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