Onasemnogene Abeparvovec in Type 1 Spinal Muscular Atrophy: A Systematic Review and Meta-Analysis-Reference-Cited by-同舟云学术

Onasemnogene Abeparvovec in Type 1 Spinal Muscular Atrophy: A Systematic Review and Meta-Analysis

Published:2023-02-01 Issue:3-4 Volume:34 Page:129-138
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Pascual-Morena Carlos¹,Cavero-Redondo Iván²^ORCID,Lucerón-Lucas-Torres Maribel¹,Martínez-García Irene¹,Rodríguez-Gutiérrez Eva¹,Martínez-Vizcaíno Vicente¹²

Affiliation:

1. Health and Social Research Center, Universidad de Castilla—La Mancha, Cuenca, Spain

2. Facultad de Ciencias de la Salud, Universidad Autónoma de Chile, Talca, Chile.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2022.161

Reference48 articles.

1. Spinal muscular atrophy

2. Genetic risk assessment in carrier testing for spinal muscular atrophy

3. Newborn and carrier screening for spinal muscular atrophy

4. The role of survival motor neuron protein (SMN) in protein homeostasis

5. Diagnosis and management of spinal muscular atrophy: Part 1: Recommendations for diagnosis, rehabilitation, orthopedic and nutritional care

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3. Efficacy and safety of onasemnogene abeparvovec for the treatment of patients with spinal muscular atrophy type 1: A systematic review with meta-analysis;PLOS ONE;2024-05-07

4. Spinal Muscular Atrophy Types, Innovations in Diagnosis and Treatment;Journal of Dr Behcet Uz Children s Hospital;2023-12-04

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