An Engineered Adeno-Associated Virus Capsid Mediates Efficient Transduction of Pericytes and Smooth Muscle Cells of the Brain Vasculature-Reference-Cited by-同舟云学术

An Engineered Adeno-Associated Virus Capsid Mediates Efficient Transduction of Pericytes and Smooth Muscle Cells of the Brain Vasculature

Published:2023-08-01 Issue:15-16 Volume:34 Page:682-696
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Ramirez Servio H.¹²,Hale Jonathan F.¹²,McCarthy Siobhan³,Lino Cardenas Christian L.⁴⁵,Dona Kalpani N. Udeni Galpayage¹²,Hanlon Killian S.⁴⁶,Hudry Eloise⁴⁶,Cruz Demitri De La⁴⁶⁷,Ng Carrie⁴⁶⁷,Das Sabyasachi³,Nguyen Diane M.⁶,Nammour Josette⁴⁶⁷,Bennett Rachel E.⁴⁶,Andrews Allison M.¹²,Musolino Patricia L.³⁴⁶,Maguire Casey A.⁴⁶⁷^ORCID

Affiliation:

1. Department of Pathology and Laboratory Medicine, Temple University School of Medicine, Philadelphia, Pennsylvania, USA.

2. Shriners Hospitals Pediatric Research Center, Philadelphia, Pennsylvania, USA.

3. Center for Genomic Medicine; Massachusetts General Hospital, Boston, Massachusetts, USA.

4. Harvard Medical School, Boston, Massachusetts, USA.

5. Department of Cardiology; Massachusetts General Hospital, Boston, Massachusetts, USA.

6. Department of Neurology; Massachusetts General Hospital, Boston, Massachusetts, USA.

7. Molecular Neurogenetics Unit, Massachusetts General Hospital, Charlestown, Massachusetts, USA.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2022.211

Reference36 articles.

1. The role of brain vasculature in neurodegenerative disorders

2. Genetics of Cerebral Small Vessel Disease

3. Monogenic Causes of Strokes

4. Cerebrovascular Disease Progression in Patients With ACTA2 Arg179 Pathogenic Variants

5. Intravascular AAV9 preferentially targets neonatal neurons and adult astrocytes

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