Sustained Reduction of Hyperbilirubinemia in Gunn Rats After Adeno-Associated Virus-Mediated Gene Transfer of Bilirubin UDP-Glucuronosyltransferase Isozyme 1A1 to Skeletal Muscle-Reference-Cited by-同舟云学术

Sustained Reduction of Hyperbilirubinemia in Gunn Rats After Adeno-Associated Virus-Mediated Gene Transfer of Bilirubin UDP-Glucuronosyltransferase Isozyme 1A1 to Skeletal Muscle

Published:2012-10 Issue:10 Volume:23 Page:1082-1089
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Pastore Nunzia¹,Nusco Edoardo¹,Vaníkova Jana²,Sepe Rosa Maria¹,Vetrini Francesco¹,McDonagh Antony³,Auricchio Alberto¹⁴⁵,Vitek Libor²⁶,Brunetti-Pierri Nicola¹⁵

Affiliation:

1. Telethon Institute of Genetics and Medicine (TIGEM), 80131 Naples, Italy.

2. Institute of Clinical Biochemistry and Laboratory Medicine, First Faculty of Medicine, Charles University, 120 00 Prague, Czech Republic.

3. University of California San Francisco (UCSF), San Francisco, CA 94143.

4. Medical Genetics, Department of Pediatrics, Federico II University of Naples, 80131 Naples, Italy.

5. Department of Pediatrics, Federico II University of Naples, 80131 Naples, Italy.

6. Fourth Department of Internal Medicine, First Faculty of Medicine, Charles University, 120 00 Prague, Czech Republic.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2012.018

Reference45 articles.

1. Chronic nonhemolytic unconjugated hyperbilirubinemia with glucuronyl transferase deficiency

2. Safety and efficacy of factor IX gene transfer to skeletal muscle in murine and canine hemophilia B models by adeno-associated viral vector serotype 1

3. Peripheral transvenular delivery of adeno-associated viral vectors to skeletal muscle as a novel therapy for hemophilia B

4. Hyaluronan in Peritumoral Stroma and Malignant Cells Associates with Breast Cancer Spreading and Predicts Survival

Cited by 9 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. ER Disposal Pathways in Chronic Liver Disease: Protective, Pathogenic, and Potential Therapeutic Targets;Frontiers in Molecular Biosciences;2022-01-31

2. Low efficacy of recombinant SV40 in Ugt1a1-/- mice with severe inherited hyperbilirubinemia;PLOS ONE;2021-04-23

3. Genetic-Based Approaches to Inherited Metabolic Liver Diseases;Human Gene Therapy;2019-10-01

4. Crigler-Najjar Syndrome: Current Perspectives and the Application of Clinical Genetics;Endocrine, Metabolic & Immune Disorders - Drug Targets;2018-04-02

5. Bilirubin Metabolism and Its Disorders;Zakim and Boyer's Hepatology;2018