Gene Therapy of Inherited Retinopathies: A Long and Successful Road from Viral Vectors to Patients
Author:
Affiliation:
1. Telethon Institute of Genetics and Medicine (TIGEM), 80131 Naples, Italy.
2. Medical Genetics, Department of Pediatrics, Federico II University, 80131 Naples, Italy.
Publisher
Mary Ann Liebert Inc
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.liebertpub.com/doi/pdf/10.1089/hum.2012.123
Reference164 articles.
1. Gene therapy restores vision in a canine model of childhood blindness
2. Impairment of the Transient Pupillary Light Reflex inRpe65−/−Mice and Humans with Leber Congenital Amaurosis
3. Restoration of cone vision in a mouse model of achromatopsia
4. Restoration of photoreceptor ultrastructure and function in retinal degeneration slow mice by gene therapy
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