Correction of Brain Oligodendrocytes by AAVrh.10 Intracerebral Gene Therapy in Metachromatic Leukodystrophy Mice-Reference-Cited by-同舟云学术

Correction of Brain Oligodendrocytes by AAVrh.10 Intracerebral Gene Therapy in Metachromatic Leukodystrophy Mice

Published:2012-08 Issue:8 Volume:23 Page:903-914
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Piguet Françoise¹,Sondhi Dolan²,Piraud Monique³,Fouquet Françoise¹,Hackett Neil R.²,Ahouansou Ornella¹,Vanier Marie-Thérèse⁴,Bieche Ivan¹,Aubourg Patrick¹⁵,Crystal Ronald G.²,Cartier Nathalie¹,Sevin Caroline¹⁵

Affiliation:

1. INSERM U745, University Paris-Descartes, 75005, Paris, France.

2. Department of Genetic Medicine, Weill Cornell Medical College, New York, NY 10065.

3. Centre de Biologie et de Pathologie Est, Lyon Hospital, 69677, Bron, France.

4. INSERM U820, 69372, Lyon, France.

5. Bicêtre Hospital, Neuropediatrics Unit, Le Kremlin Bicêtre, 94275, Paris, France.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2012.015

Reference46 articles.

1. Widespread cortical expression of MANF by AAV serotype 7: Localization and protection against ischemic brain injury

2. A pedigree study of metachromatic leukodystrophy: Biochemical identification of the carrier state

3. Correction of metachromatic leukodystrophy in the mouse model by transplantation of genetically modified hematopoietic stem cells

4. Gene therapy of metachromatic leukodystrophy reverses neurological damage and deficits in mice

5. Early marrow transplantation in a pre-symptomatic neonate with late infantile metachromatic leukodystrophy does not halt disease progression

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