Gene Therapy Approaches for Lysosomal Storage Disease: Next-Generation Treatment
Author:
Affiliation:
1. Department of Pediatrics and Powell Gene Therapy Center, University of Florida, Gainesville, FL 32610.
Publisher
Mary Ann Liebert Inc
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.liebertpub.com/doi/pdf/10.1089/hum.2012.140
Reference72 articles.
1. Progress and Prospects: Gene Therapy Clinical Trials (Part 1)
2. Strategies to Modulate Immune Responses: A New Frontier for Gene Therapy
3. Systemic Gene Delivery in Large Species for Targeting Spinal Cord, Brain, and Peripheral Tissues for Pediatric Disorders
4. Comparison of ventricular and intravenous lentiviral-mediated gene therapy for murine MPS VII
5. Gene Therapy of Storage Disorders by Retroviral and Lentiviral Vectors
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