Antisense Oligonucleotides for the Treatment of Spinal Muscular Atrophy
Author:
Affiliation:
1. Department of Molecular and Cellular Biochemistry, The Ohio State University, Columbus, OH 43210.
2. Department of Neurological Surgery, The Ohio State University Medical Center, Columbus, OH 43210.
Publisher
Mary Ann Liebert Inc
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.liebertpub.com/doi/pdf/10.1089/hum.2012.225
Reference101 articles.
1. Finger Cold-Induced Vasodilatation, Sympathetic Skin Response, and R—R Interval Variation in Patients With Progressive Spinal Muscular Atrophy
2. Vascular Perfusion Abnormalities in Infants with Spinal Muscular Atrophy
3. Medical Considerations of Long-Term Survival of Werdnig–Hoffmann Disease
4. Delivery of bifunctional RNAs that target an intronic repressor and increase SMN levels in an animal model of spinal muscular atrophy
5. Alternative Splicing Events Are a Late Feature of Pathology in a Mouse Model of Spinal Muscular Atrophy
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