Adeno-Associated Virus Vector-Mediated Minidystrophin Gene Therapy Improves Dystrophic Muscle Contractile Function inmdxMice-Reference-Cited by-同舟云学术

Adeno-Associated Virus Vector-Mediated Minidystrophin Gene Therapy Improves Dystrophic Muscle Contractile Function inmdxMice

Published:2002-08-10 Issue:12 Volume:13 Page:1451-1460
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Watchko Jon¹,O'Day Terry¹,Wang Bing²,Zhou Liqiao²,Tang Ying²,Li Juan²,Xiao Xiao³

Affiliation:

1. Division of Neonatology and Developmental Biology, Department of Pediatrics, Magee-Women's Research Institute, Pittsburgh, PA 15213

2. Department of Molecular Genetics and Biochemistry, University of Pittsburgh School of Medicine, Pittsburgh, PA 15261

3. Department of Molecular Genetics and Biochemistry, University of Pittsburgh School of Medicine, Pittsburgh, PA 15261 and Department of Orthopedic Surgery, University of Pittsburgh School of Medicine, Pittsburgh, PA 15261

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/10430340260185085

Reference56 articles.

1. Human dystrophin expression in mdx mice after intramuscular injection of DNA constructs

2. In vivo targeted repair of a point mutation in the canine dystrophin gene by a chimeric RNA/DNA oligonucleotide

3. Persistent expression of canine factor IX in hemophilia B canines

4. Several Log Increase in Therapeutic Transgene Delivery by Distinct Adeno-Associated Viral Serotype Vectors

5. Sustained and Complete Phenotype Correction of Hemophilia B Mice Following Intramuscular Injection of AAV1 Serotype Vectors

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