Recombinant Adeno-Associated Virus-Mediated Correction of Lysosomal Storage within the Central Nervous System of the Adult Mucopolysaccharidosis Type VII Mouse-Reference-Cited by-同舟云学术

Recombinant Adeno-Associated Virus-Mediated Correction of Lysosomal Storage within the Central Nervous System of the Adult Mucopolysaccharidosis Type VII Mouse

Published:2000-03 Issue:4 Volume:11 Page:507-519
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Sferra Thomas J.,Qu Guang,McNeely David,Rennard Rachel,Clark K. Reed,Lo Warren D.,Johnson Philip R.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/10430340050015707

Reference61 articles.

1. Human β-GIucuronidase. II. Fate of Infused Human Placental β-Glucuronidase in the Rat

2. Human β-glucuronidase: In vivo clearance and in vitro uptake by a glycoprotein recognition system on reticuloendothelial cells

3. Effects of Gamma Irradiation on the Transduction of Dividing and Nondividing Cells in Brain and Muscle of Rats by Adeno-Associated Virus Vectors

4. Fluorescent viral vectors: A new technique for the pharmacological analysis of gene therapy

5. Behavioral consequences of bone marrow transplantation in the treatment of murine mucopolysaccharidosis type VII.

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