Adeno-Associated Virus Type 5: Transduction Efficiency and Cell-Type Specificity in the Primate Retina-Reference-Cited by-同舟云学术

Adeno-Associated Virus Type 5: Transduction Efficiency and Cell-Type Specificity in the Primate Retina

Published:2003-11-20 Issue:17 Volume:14 Page:1663-1671
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Lotery Andrew J.¹,Yang Grace S.²,Mullins Robert F.¹,Russell Stephen R.¹,Schmidt Michael³,Stone Edwin M.⁴,Lindbloom Jonathan D.⁵,Chiorini John A.⁶,Kotin Robert M.³,Davidson Beverly L.⁷

Affiliation:

1. Department of Ophthalmology, Roy J. and Lucille A Carver College of Medicine, Iowa City, IA 52242

2. Department of Otolaryngology, Roy J. and Lucille A Carver College of Medicine, Iowa City, IA 52242

3. National Heart, Lung, and Blood Institute, Bethesda, MD 20892

4. Department of Ophthalmology and Howard Hughes Medical Institute, Roy J. and Lucille A Carver College of Medicine, Iowa City, IA 52242

5. Department of Internal Medicine, Roy J. and Lucille A Carver College of Medicine, Iowa City, IA 52242

6. Gene Therapy and Therapeutics Branch, NIDCR, Bethesda, MD 20892

7. Departments of Internal Medicine, Neurology and Physiology & Biophysics, Roy J. and Lucille A Carver College of Medicine, Iowa City, IA 52242

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/104303403322542301

Reference26 articles.

1. Gene therapy restores vision in a canine model of childhood blindness

2. Restoration of photoreceptor ultrastructure and function in retinal degeneration slow mice by gene therapy

3. Stable transgene expression in rod photoreceptors after recombinant adeno-associated virus-mediated gene transfer to monkey retina

4. Effects of Adeno-associated Virus-vectored Ciliary Neurotrophic Factor on Retinal Structure and Function in Mice with a P216L rds/peripherin Mutation

5. Cloning and Characterization of Adeno-Associated Virus Type 5

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