Bone Marrow Stem Cell Gene Therapy of Arylsulfatase A-Deficient Mice, Using an Arylsulfatase A Mutant That Is Hypersecreted from Retrovirally Transduced Donor-Type Cells-Reference-Cited by-同舟云学术

Bone Marrow Stem Cell Gene Therapy of Arylsulfatase A-Deficient Mice, Using an Arylsulfatase A Mutant That Is Hypersecreted from Retrovirally Transduced Donor-Type Cells

Published:2001-06-10 Issue:9 Volume:12 Page:1021-1033
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Matzner Ulrich¹,Schestag Frank¹,Hartmann Dieter²,Lüllmann-Rauch Renate²,D'Hooge Rudi³,De Deyn Peter P.³,Gieselmann Volkmar¹

Affiliation:

1. Institut für Physiologische Chemie, Rheinische Friedrich-Wilhelms-Universität, D-53115 Bonn, Germany

2. Anatomisches Institut, Christian-Albrechts-Universität, D-24114 Kiel, Germany

3. Laboratory of Neurochemistry and Behavior, Born Bunge Foundation, University of Antwerp, B-2610 Antwerp, Belgium

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/104303401750214258

Reference38 articles.

1. Normal Lysosomal Morphology and Function in LAMP-1-deficient Mice

2. The assay of arylsulphatases A and B in human urine

3. Increased life span and correction of metabolic defects in murine mucopolysaccharidosis type VII after syngeneic bone marrow transplantation

4. Lysosomal storage diseases: mechanisms of enzyme replacement therapy

5. Mannose 6-phosphate receptor dependent secretion of lysosomal enzymes.

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