A Simplified Approach to Improve the Efficiency and Safety ofEx VivoHematopoietic Gene Therapy in Fanconi Anemia Patients-Reference-Cited by-同舟云学术

A Simplified Approach to Improve the Efficiency and Safety ofEx VivoHematopoietic Gene Therapy in Fanconi Anemia Patients

Published:2006-02 Issue:2 Volume:17 Page:245-250
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Jacome A.¹²,Navarro S.¹³,Casado J.A.¹³,Rio P.¹³,Madero L.¹⁴,Estella J.¹⁵,Sevilla J.¹⁴,Badell I.¹⁶,Ortega J.J.¹⁷,Olivé T.¹⁷,Hanenberg H.⁸,Segovia J.C.¹³,Bueren J.A.¹³

Affiliation:

1. Spanish Fanconi Anemia Research Network, Madrid 28040, Spain.

2. Hematopoiesis and Gene Therapy Division, Centro de Investigaciones Energéticas, Medioambientales, y Tecnológicas (CIEMAT)/Fundación. Marcelino Botin, Madrid 28040, Spain.

3. Hematopoiesis and Gene Therapy Division, Centro de Investigaciones Energéticas, Medioambientales, y Tecnológicas (CIEMAT)/Fundación Marcelino Botin, Madrid 28040, Spain.

4. Department of Pediatric Oncohematology, Hospital del Niño Jesús, Madrid 28009, Spain.

5. Department of Pediatric Oncohematology, Hospital San Juan de Dios, Barcelona 08950, Spain.

6. Department of Pediatric Oncohematology, Hospital de la Santa Creu i Sant Pau, Barcelona 08025, Spain.

7. Department of Pediatric Oncohematology, Hospital Vall dHebrón, Barcelona 08035, Spain.

8. Department of Pediatric Oncology, Hematology and Immunology, Children's Hospital, Heinrich Heine University, 40225 Düsseldorf, Germany.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2006.17.245

Reference28 articles.

1. Correction of ADA-SCID by Stem Cell Gene Therapy Combined with Nonmyeloablative Conditioning

2. Progressive Telomere Shortening in Aplastic Anemia

3. Breaks at telomeres and TRF2-independent end fusions in Fanconi anemia

4. Gene Therapy of Human Severe Combined Immunodeficiency (SCID)-X1 Disease

5. Mobilization and collection of peripheral blood CD34+ cells from patients with Fanconi anemia

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