Evaluation of Primitive Murine Hematopoietic Stem and Progenitor Cell Transduction In Vitro and In Vivo by Recombinant Adeno-Associated Virus Vector Serotypes 1 Through 5-Reference-Cited by-同舟云学术

Evaluation of Primitive Murine Hematopoietic Stem and Progenitor Cell Transduction In Vitro and In Vivo by Recombinant Adeno-Associated Virus Vector Serotypes 1 Through 5

Published:2006-03 Issue:3 Volume:17 Page:321-333
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Zhong Li¹,Li Weiming²,Li Yanjun³⁴,Zhao Weihong¹⁵,Wu Jianqing¹⁵,Li Baozheng¹,Maina Njeri¹⁶,Bischof Daniela⁶,Qing Keyun⁷,Weigel-Kelley Kirsten A.¹,Zolotukhin Irene¹,Warrington Kenneth H.¹,Li Xiaomiao⁸,Slayton William B.⁸,Yoder Mervin C.³,Srivastava Arun¹

Affiliation:

1. Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida College of Medicine, Gainesville, FL 32610.

2. Herman B. Wells Center for Pediatric Research and Department of Biochemistry and Molecular Biology, Indiana University School of Medicine, Indianapolis, IN 46202. 3Eli Lilly & Co., Indianapolis, IN 46285.

3. Herman B. Wells Center for Pediatric Research and Department of Biochemistry and Molecular Biology, Indiana University School of Medicine, Indianapolis, IN 46202.

4. Department of Pharmaceutics, University of Florida College of Pharmacy, Gainesville, FL 32610.

5. The First Affiliated Hospital of Nanjing Medical University, Nanjing, Jiangsu, P.R. China 210029.

6. Department of Microbiology and Immunology, Indiana University School of Medicine, Indianapolis, IN 46202.

7. Eli Lilly & Co., Indianapolis, IN 46285.

8. Division of Hematology/Oncology, Department of Pediatrics, University of Florida College of Medicine, Gainesville, FL 32610.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2006.17.321

Reference73 articles.

1. A Phase I Study of Aerosolized Administration of tgAAVCF to Cystic Fibrosis Subjects with Mild Lung Disease

2. Transfer of Contaminants in Adeno-Associated Virus Vector Stocks Can Mimic Transduction and Lead to Artifactual Results

3. Safety and efficacy of factor IX gene transfer to skeletal muscle in murine and canine hemophilia B models by adeno-associated viral vector serotype 1

4. Developmental analysis of the cytomegalovirus enhancer in transgenic animals

5. The enhancer domain of the human cytomegalovirus major immediate-early promoter determines cell type-specific expression in transgenic mice

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