Correction of Feline Lipoprotein Lipase Deficiency with Adeno-Associated Virus Serotype 1-Mediated Gene Transfer of the Lipoprotein Lipase S447X Beneficial Mutation

Author:

Ross Colin J.D.1,Twisk Jaap2,Bakker Andrew C.2,Miao Fudan1,Verbart Dennis2,Rip Jaap3,Godbey Tamara4,Dijkhuizen Paul2,Hermens Wim T.J.M.C.2,Kastelein John J.P.3,Kuivenhoven Jan Albert3,Meulenberg Janneke M.2,Hayden Michael R.1

Affiliation:

1. Department of Medical Genetics, University of British Columbia, and Centre for Molecular Medicine and Therapeutics, Vancouver, BC, Canada V5Z 4H4.

2. Amsterdam Molecular Therapeutics, 1105-BA Amsterdam, The Netherlands.

3. Department of Vascular Medicine, Academic Medical Center, University of Amsterdam, 1100-DE Amsterdam, The Netherlands.

4. Animal Care Centre, University of British Columbia, Vancouver, BC, Canada V6T 1W5.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

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