Global Seroprevalence of Pre-existing Immunity Against AAV5 and Other AAV Serotypes in People with Hemophilia A

Author:

Klamroth Robert1ORCID,Hayes Gregory2,Andreeva Tatiana3,Gregg Keith2,Suzuki Takashi4,Mitha Ismail Haroon5,Hardesty Brandon6,Shima Midori7,Pollock Toni8,Slev Patricia8,Oldenburg Johannes9,Ozelo Margareth C.10,Stieltjes Natalie11,Castet Sabine-Marie12,Mahlangu Johnny13,Peyvandi Flora1415,Kazmi Rashid16,Schved Jean-François17,Leavitt Andrew D.18,Callaghan Michael19,Pan-Petesch Brigitte20,Quon Doris V.21,Andrews Jayson2,Trinh Alex2,Li Mingjin2,Wong Wing Yen2

Affiliation:

1. Comprehensive Care Haemophilia Treatment Center, Vivantes Klinikum im Friedrichshain, Berlin, Germany

2. BioMarin Pharmaceutical, Inc., Novato, California, USA

3. Municipal Center of Hemophilia Therapy, Saint Petersburg, Russia

4. Ogikubo Hospital, Tokyo, Japan

5. Worthwhile Clinical Trials, Lakeview Hospital, Benoni, South Africa

6. Indiana Hemophilia and Thrombosis Center, Indianapolis, Indiana, USA

7. Nara Medical University, Kashihara, Japan

8. ARUP Laboratories, Salt Lake City, Utah, USA

9. Universitätsklinikum Bonn, Bonn, Germany

10. Hemocentro UNICAMP, Department of Internal Medicine, School of Medical Sciences, University of Campinas, Campinas, Brazil

11. Department of Haematology and Regional Centre of Haemophilia Treatment, Hôpital Cochin, Assistance Publique Hôpitaux de Paris (AP-HP), Sorbonne Paris Cité, Université Paris Descartes, Paris, France

12. Centre de Ressources et de Compétence des Maladies Hémorragiques Constitutionnelles, CHU de Bordeaux, Bordeaux, France

13. Haemophilia Comprehensive Care Centre, University of the Witwatersrand and National Health Laboratory Service, Johannesburg, South Africa

14. Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy

15. Department of Pathophysiology and Transplantation, Università degli Studi di Milano, Milan, Italy

16. Department of Haematology, Southampton University Hospital, Southampton, United Kingdom

17. Centre Régional de Traitement des Hémophiles, Hôpital Saint-Eloi, CHRU de Montpellier, Montpellier, France

18. Departments of Medicine and Laboratory Medicine, University of California San Francisco, San Francisco, California, USA

19. Division of Pediatric Hematology/Oncology, Central Michigan University, Detroit, Michigan, USA

20. Centre Hospitalier Régional Universitaire de Brest, Hôpital A. Morvan, Brest, France

21. Orthopaedic Hemophilia Treatment Center, Orthopaedic Institute for Children, Los Angeles, California, USA.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

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