Targeting NSG Mice Engrafting Cells with a Clinically Applicable Lentiviral Vector Corrects Osteoclasts in Infantile Malignant Osteopetrosis-Reference-Cited by-同舟云学术

Targeting NSG Mice Engrafting Cells with a Clinically Applicable Lentiviral Vector Corrects Osteoclasts in Infantile Malignant Osteopetrosis

Published:2018-08 Issue:8 Volume:29 Page:938-949
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Moscatelli Ilana¹,Löfvall Henrik¹²,Schneider Thudium Christian²,Rothe Michael³,Montano Carmen¹,Kertész Zsuzsanna¹,Sirin Mehtap⁴,Schulz Ansgar⁴,Schambach Axel³,Henriksen Kim²,Richter Johan¹

Affiliation:

1. Department of Molecular Medicine and Gene Therapy, Lund Strategic Center for Stem Cell Biology, Lund University, Lund, Sweden

2. Nordic Bioscience, Herlev, Denmark

3. Institute of Experimental Hematology, Hannover Medical School, Hannover, Germany

4. Department of Pediatrics and Adolescent Medicine, University Medical Center, Ulm, Germany.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2017.053

Reference31 articles.

1. Advances in osteoclast biology resulting from the study of osteopetrotic mutations

2. Osteopetrosis

3. Genotype-Phenotype Relationship in Human ATP6i-Dependent Autosomal Recessive Osteopetrosis

4. Lentiviral gene transfer of TCIRG1 into peripheral blood CD34+ cells restores osteoclast function in infantile malignant osteopetrosis

5. Defects in TCIRG1 subunit of the vacuolar proton pump are responsible for a subset of human autosomal recessive osteopetrosis

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