Comparison of Zinc Finger Nucleases Versus CRISPR-Specific Nucleases for Genome Editing of the Wiskott-Aldrich Syndrome Locus-Reference-Cited by-同舟云学术

Comparison of Zinc Finger Nucleases Versus CRISPR-Specific Nucleases for Genome Editing of the Wiskott-Aldrich Syndrome Locus

Published:2018-03 Issue:3 Volume:29 Page:366-380
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Gutierrez-Guerrero Alejandra¹,Sanchez-Hernandez Sabina¹,Galvani Giuseppe¹,Pinedo-Gomez Javier¹,Martin-Guerra Rocio¹,Sanchez-Gilabert Almudena¹,Aguilar-González Araceli¹,Cobo Marién¹²,Gregory Philip³,Holmes Michael³,Benabdellah Karim¹²,Martin Francisco¹²

Affiliation:

1. Centre for Genomics and Oncological Research (GENYO), Pfizer/University of Granada/Andalusian Regional Government, Genomic Medicine Department, Granada, Spain

2. LentiStem Biotech, Granada, Spain

3. Sangamo BioSciences, Point Richmond Tech Center, Richmond, California.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2017.047

Reference63 articles.

1. Wiskott-Aldrich syndrome: a comprehensive review

2. Wiskott–Aldrich syndrome: a gene, a multifunctional protein and the beginnings of an explanation

3. Mutations of the Wiskott-Aldrich Syndrome Protein (WASP): hotspots, effect on transcription, and translation and phenotype/genotype correlation