Approaches for Systemic Delivery of Dystrophin Antisense Peptide Nucleic Acid in the mdx Mouse Model-Reference-Cited by-同舟云学术

Approaches for Systemic Delivery of Dystrophin Antisense Peptide Nucleic Acid in the mdx Mouse Model

Published:2021-06-01 Issue:3 Volume:31 Page:208-219
ISSN:2159-3337
Container-title:Nucleic Acid Therapeutics
language:en
Short-container-title:Nucleic Acid Therapeutics

Author:

Brolin Camilla¹,Lim Ernest Wee Kiat¹,Grizot Sylvestre²,Olsen Caroline Holkmann³,Yavari Niloofar¹,Krag Thomas O.⁴,Nielsen Peter E.¹

Affiliation:

1. Department of Cellular and Molecular Medicine, Faculty of Health and Medical Sciences, The Panum Institute, University of Copenhagen, Copenhagen, Denmark.

2. MedinCell, Jacou, France.

3. Department of Pathology, Rigshospitalet, Copenhagen, Denmark.

4. Department of Neurology, Copenhagen Neuromuscular Center, Rigshospitalet, University of Copenhagen, Copenhagen, Denmark.

Publisher

Mary Ann Liebert Inc

Subject

Drug Discovery,Genetics,Molecular Biology,Molecular Medicine,Biochemistry

Link

https://www.liebertpub.com/doi/pdf/10.1089/nat.2020.0856

Reference22 articles.

1. Peptide nucleic acid (PNA) and its applications in chemical biology, diagnostics, and therapeutics

2. In vivo correction of anaemia in β-thalassemic mice by γPNA-mediated gene editing with nanoparticle delivery

3. MicroRNA silencing for cancer therapy targeted to the tumour microenvironment

4. Systemically delivered antisense oligomers upregulate gene expression in mouse tissues

Cited by 7 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. A review on mechanistic insights into structure and function of dystrophin protein in pathophysiology and therapeutic targeting of Duchenne muscular dystrophy;International Journal of Biological Macromolecules;2024-04

2. Polymeric in situ forming depots for long-acting drug delivery systems;Advanced Drug Delivery Reviews;2023-09

3. Thyclotides, tetrahydrofuran-modified peptide nucleic acids that efficiently penetrate cells and inhibit microRNA-21;Nucleic Acids Research;2022-10-10

4. Antisense Peptide Nucleic Acid–Diaminobutanoic Acid Dendron Conjugates with SbmA-Independent Antimicrobial Activity against Gram-Negative Bacteria;ACS Infectious Diseases;2022-04-18

5. Mechanisms and applications of peptide nucleic acids selectively binding to double‐stranded RNA;Biopolymers;2021-09-28