The 10th Oligonucleotide Therapy Approved: Golodirsen for Duchenne Muscular Dystrophy
Author:
Affiliation:
1. Department of Human Genetics, Leiden University Medical Center, Leiden, the Netherlands.
2. Department of Pharmacology, UT Southwestern Medical Center, Dallas, Texas.
3. Department of Biochemistry, UT Southwestern Medical Center, Dallas, Texas.
Publisher
Mary Ann Liebert Inc
Subject
Drug Discovery,Genetics,Molecular Biology,Molecular Medicine,Biochemistry
Link
https://www.liebertpub.com/doi/pdf/10.1089/nat.2020.0845
Reference14 articles.
1. The TREAT-NMD DMD Global Database: Analysis of More than 7,000 Duchenne Muscular Dystrophy Mutations
2. Theoretic applicability of antisense-mediated exon skipping for Duchenne muscular dystrophy mutations
3. FDA Approves Eteplirsen for Duchenne Muscular Dystrophy: The Next Chapter in the Eteplirsen Saga
4. Eteplirsen treatment for Duchenne muscular dystrophy
5. Why dystrophin quantification is key in the eteplirsen saga
Cited by 81 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献
1. Duchenne muscular dystrophy: promising early-stage clinical trials to watch;Expert Opinion on Investigational Drugs;2024-01-30
2. Splice-Modulating Antisense Oligonucleotides as Therapeutics for Inherited Metabolic Diseases;BioDrugs;2024-01-22
3. Nurturing longevity through natural compounds: Where do we stand, and where do we go?;Food Frontiers;2024-01-10
4. Nucleic acid degradation as barrier to gene delivery: a guide to understand and overcome nuclease activity;Chemical Society Reviews;2024
5. Recent applications of RNA therapeutic in clinics;Progress in Molecular Biology and Translational Science;2024
1.学者识别学者识别
2.学术分析学术分析
3.人才评估人才评估
"同舟云学术"是以全球学者为主线,采集、加工和组织学术论文而形成的新型学术文献查询和分析系统,可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容,当前同舟云学术共收录了国内外主流学术期刊6万余种,收集的期刊论文及会议论文总量共计约1.5亿篇,并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询!咨询电话:010-8811{复制后删除}0370
www.globalauthorid.com
TOP
Copyright © 2019-2024 北京同舟云网络信息技术有限公司 京公网安备11010802033243号 京ICP备18003416号-3