A Phase I Study of an Adeno-Associated Virus-CFTR Gene Vector in Adult CF Patients with Mild Lung Disease. Johns Hopkins Children's Center, Baltimore, Maryland-Reference-Cited by-同舟云学术

A Phase I Study of an Adeno-Associated Virus-CFTR Gene Vector in Adult CF Patients with Mild Lung Disease. Johns Hopkins Children's Center, Baltimore, Maryland

Published:1996-06-10 Issue:9 Volume:7 Page:1145-1159
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Flotte Terence,Carter Barrie,Conrad Carol,Guggino William,Reynolds Thomas,Rosenstein Beryl,Taylor George,Walden Sandra,Wetzel Randall

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.1996.7.9-1145

Reference12 articles.

1. Cystic fibrosis: molecular biology and therapeutic implications

2. Cystic fibrosis: a disease in electrolyte transport

3. Altered chloride ion channel kinetics associated with the ΔF508 cystic fibrosis mutation

4. Identification of the Cystic Fibrosis Gene: Cloning and Characterization of Complementary DNA

5. Defective regulation of outwardly rectifying Cl− channels by protein kinase A corrected by insertion of CFTR

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