1. Faculty of Medicine and Health, School of Medical Sciences, The University of Sydney, Sydney, Australia; Military Institute of Medicine, Warsaw, Poland.
2. Molecular Neurobiology Research Laboratory, Kid's Research, Westmead, Australia; Military Institute of Medicine, Warsaw, Poland.
3. Kids Neuroscience Centre, Kids Research, Children's Hospital at Westmead, Westmead, Australia; Military Institute of Medicine, Warsaw, Poland.
4. Genetic Metabolic Disorders Service, Sydney Children's Hospital Network Sydney, Westmead, Australia; Military Institute of Medicine, Warsaw, Poland.
5. Discipline of Child and Adolescent Health, Faculty of Medicine and Health, The University of Sydney, Sydney, Australia; Military Institute of Medicine, Warsaw, Poland.
6. Division of Cancer and Genetics, School of Medicine, Cardiff University, Cardiff, United Kingdom; Military Institute of Medicine, Warsaw, Poland.
7. Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, Australia; Military Institute of Medicine, Warsaw, Poland.
8. Vector and Genome Engineering Facility, Children's Medical Research Institute, The University of Sydney, Westmead, Australia; and Military Institute of Medicine, Warsaw, Poland.
9. Laboratory of Molecular Oncology and Innovative Therapies, Military Institute of Medicine, Warsaw, Poland.
10. Children's Medical Research Institute, Westmead, Australia; Military Institute of Medicine, Warsaw, Poland.