Comparison of Retroviral and Adeno-Associated Viral Vectors Designed to Express Human Clotting Factor IX
Author:
Publisher
Mary Ann Liebert Inc
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.liebertpub.com/doi/pdf/10.1089/hum.1997.8.2-125
Reference33 articles.
1. R-Region cDNA Inserts in Retroviral Vectors Are Compatible with Virus Replication and High-Level Protein Synthesis from the Insert
2. Phenotypic correction of factor IX deficiency in skin fibroblasts of hemophilic dogs.
3. Development of a high-titer retrovirus producer cell line capable of gene transfer into rhesus monkey hematopoietic stem cells.
4. Lack of expression from a retroviral vector after transduction of murine hematopoietic stem cells is associated with methylation in vivo.
5. Multiple modifications in cis elements of the long terminal repeat of retroviral vectors lead to increased expression and decreased DNA methylation in embryonic carcinoma cells
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