Retroviral Transfer of Acidα-Glucosidase cDNA to Enzyme-Deficient Myoblasts Results in Phenotypic Spread of the Genotypic Correction by Both Secretion and Fusion-Reference-Cited by-同舟云学术

Retroviral Transfer of Acidα-Glucosidase cDNA to Enzyme-Deficient Myoblasts Results in Phenotypic Spread of the Genotypic Correction by Both Secretion and Fusion

Published:1997-09 Issue:13 Volume:8 Page:1555-1563
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Zaretsky Joseph Z.,Candotti Fabio,Boerkoel Cornelius,Adams Elizabeth M.,Yewdell Jonathan W.,Blaese R. Michael,Plotz Paul H.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.1997.8.13-1555

Reference47 articles.

1. Systemic Delivery of Recombinant Proteins by Genetically Modified Myoblasts

2. Replacement Therapy for Inherited Enzyme Deficiency — Macrophage-Targeted Glucocerebrosidase for Gaucher's Disease

3. Gaucher disease: new molecular approaches to diagnosis and treatment

4. Muscle-Mediated Gene Therapy

5. Isolation and characterization of human muscle cells.

Cited by 37 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Gene therapy for primary myopathies: literature review and prospects;Archives de Pédiatrie;2023-11

2. What’s new and what’s next for gene therapy in Pompe disease?;Expert Opinion on Biological Therapy;2022-04-27

3. Crotamine as a vehicle for non-viral gene delivery for Pompe disease;2021-03-23

4. Molecular Approaches for the Treatment of Pompe Disease;Molecular Neurobiology;2019-11-12

5. Progress and challenges of gene therapy for Pompe disease;Annals of Translational Medicine;2019-07