Gene Therapy for Fanconi Anemia: One Step Closer to the Clinic-Reference-Cited by-同舟云学术

Gene Therapy for Fanconi Anemia: One Step Closer to the Clinic

Published:2012-02 Issue:2 Volume:23 Page:141-144
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Tolar Jakub¹,Becker Pamela S.²,Clapp D. Wade³,Hanenberg Helmut³⁴,de Heredia Cristina Díaz⁵,Kiem Hans-Peter⁶,Navarro Susana⁷⁸,Qasba Pankaj⁹,Rio Paula⁷⁸,Schmidt Manfred¹⁰,Sevilla Julián¹¹,Verhoeyen Els¹²,Thrasher Adrian J.¹³¹⁴,Bueren Juan⁷⁸

Affiliation:

1. Division of Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN 55455.

2. University of Washington School of Medicine, Seattle, WA 98109.

3. Riley Hospital for Children, Indiana University School of Medicine, Indianapolis, IN 45202.

4. Department of Otorhinolaryngology, Heinrich Heine University School of Medicine, 40225 Duesseldorf, Germany.

5. Hematology and Oncology Department, Hospital Val d'Hebrón, 08035 Barcelona, Spain.

6. Fred Hutchinson Cancer Research Center, Seattle, WA 98109.

7. Hematopoiesis and Gene Therapy Division, Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas (CIEMAT), 28040 Madrid, Spain.

8. Centro de Investigación Biomédica en Red de Enfermedades Raras (CIBERER), 28040 Madrid, Spain.

9. Division of Blood Diseases and Resources, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD 20892.

10. Department of Translational Oncology, German Cancer Research Center and National Center for Tumor Diseases, 69120 Heidelberg, Germany.

11. Hemato-Oncología Pediátrica, Hospital Infantil Universitario Niño Jesús, Instituto de Investigación Sanitaria Princesa, 28009 Madrid, Spain.

12. Université de Lyon; INSERM, EVIR, U758, Human Virology Department, Ecole Normale Supérieure de Lyon, Université Lyon 1, F-69007 Lyon, France.

13. Centre for Immunodeficiency, Molecular Immunology Unit, UCL Institute of Child Health, WC1N 1EH London, United Kingdom.

14. Department of Immunology, Great Ormond Street Hospital NHS Trust, WC1N 3JH London, United Kingdom.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2011.237

Reference28 articles.

1. Preclinical correction of human Fanconi anemia complementation group A bone marrow cells using a safety-modified lentiviral vector

2. Churchill, W., and Langworth, R.M. (2008).Churchill by Himself: The Definitive Collection of Quotations. PublicAffairs, New York, p. 8.

3. Mobilization and collection of peripheral blood CD34+ cells from patients with Fanconi anemia

4. Susceptibility Pathways in Fanconi's Anemia and Breast Cancer

5. Plerixafor and G-CSF versus placebo and G-CSF to mobilize hematopoietic stem cells for autologous stem cell transplantation in patients with multiple myeloma

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