Long-Term Preservation of Cones and Improvement in Visual Function Following Gene Therapy in a Mouse Model of Leber Congenital Amaurosis Caused by Guanylate Cyclase-1 Deficiency-Reference-Cited by-同舟云学术

Long-Term Preservation of Cones and Improvement in Visual Function Following Gene Therapy in a Mouse Model of Leber Congenital Amaurosis Caused by Guanylate Cyclase-1 Deficiency

Published:2011-10 Issue:10 Volume:22 Page:1179-1190
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Mihelec Marija¹,Pearson Rachael A.¹,Robbie Scott J.¹,Buch Prateek K.¹,Azam Selina A.¹,Bainbridge James W.B.¹,Smith Alexander J.¹,Ali Robin R.¹

Affiliation:

1. Department of Genetics, University College London, Institute of Ophthalmology, London EC1V 9EL, United Kingdom.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2011.069

Reference35 articles.

1. Gene therapy restores vision in a canine model of childhood blindness

2. Restoration of cone vision in a mouse model of achromatopsia

3. Restoration of photoreceptor ultrastructure and function in retinal degeneration slow mice by gene therapy

4. Novel Adeno-Associated Virus Serotypes Efficiently Transduce Murine Photoreceptors

5. The Function of Guanylate Cyclase 1 and Guanylate Cyclase 2 in Rod and Cone Photoreceptors

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