Long-Term Systemic Myostatin Inhibition via Liver-Targeted Gene Transfer in Golden Retriever Muscular Dystrophy-Reference-Cited by-同舟云学术

Long-Term Systemic Myostatin Inhibition via Liver-Targeted Gene Transfer in Golden Retriever Muscular Dystrophy

Published:2011-12 Issue:12 Volume:22 Page:1499-1509
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Bish Lawrence T.¹,Sleeper Meg M.²,Forbes Sean C.³,Morine Kevin J.¹,Reynolds Caryn²,Singletary Gretchen E.²,Trafny Dennis²,Pham Jennifer¹,Bogan Janet⁴,Kornegay Joe N.⁴,Vandenborne Krista³,Walter Glenn A.⁵,Sweeney H. Lee¹

Affiliation:

1. Department of Physiology, University of Pennsylvania School of Medicine, Philadelphia, PA 19104.

2. Section of Cardiology, Department of Clinical Studies, Veterinary Hospital of the University of Pennsylvania, Philadelphia, PA 19104.

3. Department of Physical Therapy, University of Florida, Gainesville, FL 32610.

4. Departments of Pathology and Laboratory Medicine, Neurology, and the Gene Therapy Center, University of North Carolina–Chapel Hill, Chapel Hill, NC 27514.

5. Department of Physiology and Functional Genomics, University of Florida, Gainesville, FL 32610.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2011.102

Reference58 articles.

1. Entries in the Leiden Duchenne muscular dystrophy mutation database: An overview of mutation types and paradoxical cases that confirm the reading-frame rule

2. AAV-mediated delivery of a mutated myostatin propeptide ameliorates calpain 3 but not α-sarcoglycan deficiency

3. Muscle-specific expression of insulin-like growth factor I counters muscle decline in mdx mice

4. Evaluation of Adeno-Associated Viral Vectors for Liver-Directed Gene Transfer in Dogs

5. Functional improvement of dystrophic muscle by myostatin blockade

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