Recombinant Adeno-Associated Virus-Mediated Gene Transfer for the Potential Therapy of Adenosine Deaminase-Deficient Severe Combined Immune Deficiency-Reference-Cited by-同舟云学术

Recombinant Adeno-Associated Virus-Mediated Gene Transfer for the Potential Therapy of Adenosine Deaminase-Deficient Severe Combined Immune Deficiency

Published:2011-08 Issue:8 Volume:22 Page:935-949
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Silver Jared N.¹,Elder Melissa¹,Conlon Thomas¹,Cruz Pedro¹,Wright Amy J.¹,Srivastava Arun¹,Flotte Terence R.²

Affiliation:

1. Department of Pediatrics and Powell Gene Therapy Center, University of Florida College of Medicine, Gainesville, FL 32610.

2. Department of Pediatrics and Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA 01655.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2010.121

Reference55 articles.

1. A Phase I Study of Aerosolized Administration of tgAAVCF to Cystic Fibrosis Subjects with Mild Lung Disease

2. Gene therapy for adenosine-deaminase-deficient severe combined immunodeficiency

3. Multilineage hematopoietic reconstitution without clonal selection in ADA-SCID patients treated with stem cell gene therapy

4. Insertional mutagenesis in gene therapy and stem cell biology

5. Chance or necessity? Insertional Mutagenesis in Gene Therapy and Its Consequences

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