Safety of Liver Gene Transfer Following Peripheral Intravascular Delivery of Adeno-Associated Virus (AAV)-5 and AAV-6 in a Large Animal Model-Reference-Cited by-同舟云学术

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Safety of Liver Gene Transfer Following Peripheral Intravascular Delivery of Adeno-Associated Virus (AAV)-5 and AAV-6 in a Large Animal Model

Published:2011-07 Issue:7 Volume:22 Page:843-852
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Favaro Patricia¹,Finn Jonathan D.¹,Siner Joshua I.¹,Wright J. Fraser¹²,High Katherine A.¹³⁴,Arruda Valder R.¹³

Affiliation:

1. The Children's Hospital of Philadelphia, Philadelphia, PA 19104.

2. University of Pennsylvania Department of Pathology and Laboratory Medicine, Philadelphia, PA 19104.

3. University of Pennsylvania School of Medicine, Philadelphia, PA 19104.

4. Howard Hughes Medical Institute, Philadelphia, PA 19104.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2010.155

Reference47 articles.

1. Lack of Germline Transmission of Vector Sequences Following Systemic Administration of Recombinant AAV-2 Vector in Males

2. Peripheral transvenular delivery of adeno-associated viral vectors to skeletal muscle as a novel therapy for hemophilia B

3. Effect of Gene Therapy on Visual Function in Leber's Congenital Amaurosis

4. Percutaneous Transendocardial Delivery of Self-complementary Adeno-associated Virus 6 Achieves Global Cardiac Gene Transfer in Canines

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1. Detection of Humoral Response to Transgene Protein and Gene Editing Reagents;Drug Development for Gene Therapy;2024-02-16

2. Giroctocogene fitelparvovec gene therapy for severe hemophilia A: 104-week analysis of the Phase 1/2 Alta study;Blood Journal;2023-10-23

3. New directions to develop therapies for people with hemophilia;Expert Review of Hematology;2023-03-08

4. First-in-human in vivo genome editing via AAV-zinc-finger nucleases for mucopolysaccharidosis I/II and hemophilia B;Molecular Therapy;2022-12

5. Lack of germline transmission in male mice following a single intravenous administration of AAV5-hFVIII-SQ gene therapy;Gene Therapy;2022-02-07

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