Hereditary Inclusion Body Myopathy: Single Patient Response to Intravenous Dosing of GNE Gene Lipoplex-Reference-Cited by-同舟云学术

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Hereditary Inclusion Body Myopathy: Single Patient Response to Intravenous Dosing of GNE Gene Lipoplex

Published:2011-11 Issue:11 Volume:22 Page:1331-1341
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Nemunaitis Gregory¹²,Jay Chris M.³,Maples Phillip B.³,Gahl William A.⁴,Huizing Marjan⁴,Yardeni Tal⁴,Tong Alex W.³,Phadke Anagha P.³,Pappen Beena O.³,Bedell Cynthia¹,Allen Henry⁵,Hernandez Cathy⁵,Templeton Nancy S.³,Kuhn Joseph⁶,Senzer Neil¹³⁷,Nemunaitis John¹³⁷

Affiliation:

1. Mary Crowley Cancer Research Centers, Dallas, TX 75201.

2. MetroHealth Medical Center, Cleveland, OH 44109.

3. Gradalis, Inc., Dallas, TX 75201.

4. Medical Genetics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, MD 20892.

5. Hospitalist Internists Associates, Dallas, TX 75251.

6. WLS Surgical Associates, Dallas, TX 75246.

7. Texas Oncology, Dallas, TX 75251.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2010.192

Reference29 articles.

1. Lung Function Testing: Selection of Reference Values and Interpretative Strategies

2. Standardization of Spirometry, 1994 Update. American Thoracic Society.

3. Quantitative motor assessment in amyotrophic lateral sclerosis

4. Make Tests and Break Tests of Elbow Flexor Muscle Strength

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4. Development of Assays to Measure GNE Gene Potency and Gene Replacement in Skeletal Muscle;Journal of Neuromuscular Diseases;2023-09-08

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