Preclinical Evaluation of a Recombinant Adeno-Associated Virus Vector Expressing Human Alpha-1 Antitrypsin Made Using a Recombinant Herpes Simplex Virus Production Method-Reference-Cited by-同舟云学术

Preclinical Evaluation of a Recombinant Adeno-Associated Virus Vector Expressing Human Alpha-1 Antitrypsin Made Using a Recombinant Herpes Simplex Virus Production Method

Published:2011-02 Issue:2 Volume:22 Page:155-165
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Chulay Jeffrey D.¹,Ye Guo-Jie¹,Thomas Darby L.¹,Knop David R.¹,Benson Janet M.²,Hutt Julie A.²,Wang Gensheng²,Humphries Margaret³,Flotte Terence R.³

Affiliation:

1. Applied Genetic Technologies Corporation, Alachua, FL 32615.

2. Lovelace Biomedical and Environmental Research Institute, Albuquerque, NM 87108.

3. University of Massachusetts Medical School, Worcester, MA 01655.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2010.118

Reference31 articles.

1. Safety and Immunogenicity of Glycoprotein D--Adjuvant Genital Herpes Vaccine

2. Use of a Highly Purified α1-Antitrypsin Standard to Establish Ranges for the Common Normal and Deficient α1-Antitrypsin Phenotypes

3. Phase I Trial of Intramuscular Injection of a Recombinant Adeno-Associated Virus Serotype 2α1-Antitrypsin (AAT) Vector in AAT-Deficient Adults

4. Sustained transgene expression despite T lymphocyte responses in a clinical trial of rAAV1-AAT gene therapy

5. Sustained and Complete Phenotype Correction of Hemophilia B Mice Following Intramuscular Injection of AAV1 Serotype Vectors

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