Characterization of a Recombinant Adeno-Associated Virus Type 2 Reference Standard Material

Author:

Lock Martin1,McGorray Susan2,Auricchio Alberto34,Ayuso Eduard5,Beecham E. Jeffrey6,Blouin-Tavel Véronique7,Bosch Fatima5,Bose Mahuya8,Byrne Barry J.910,Caton Tina8,Chiorini John A.11,Chtarto Abdelwahed1213,Clark K. Reed1415,Conlon Thomas10,Darmon Christophe7,Doria Monica4,Douar Anne16,Flotte Terence R.1718,Francis Joyce D.8,Francois Achille7,Giacca Mauro19,Korn Michael T.1,Korytov Irina10,Leon Xavier5,Leuchs Barbara20,Lux Gabriele21,Melas Catherine1213,Mizukami Hiroaki22,Moullier Philippe7,Müller Marcus20,Ozawa Keiya22,Philipsberg Tina10,Poulard Karine16,Raupp Christina20,Rivière Christel16,Roosendaal Sigrid D.23,Samulski R. Jude6,Soltys Steven M.6,Surosky Richard24,Tenenbaum Liliane1213,Thomas Darby L.25,van Montfort Bart23,Veres Gabor25,Wright J. Fraser2627,Xu Yili24,Zelenaia Olga26,Zentilin Lorena19,Snyder Richard O.8928

Affiliation:

1. Gene Therapy Program, Department of Pathology and Laboratory Medicine, University of Pennsylvania, Philadelphia, PA 19104.

2. Department of Epidemiology and Health Policy Research, University of Florida College of Medicine, Gainesville, FL 32610.

3. Medical Genetics, Department of Pediatrics, Federico II University, 80131 Naples, Italy.

4. Telethon Institute of Genetics and Medicine (TIGEM), 80131 Naples, Italy.

5. Center of Animal Biotechnology and Gene Therapy and Department of Biochemistry and Molecular Biology, School of Veterinary Medicine, Universitat Autònoma de Barcelona, 08193-Bellaterra, Spain.

6. Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599.

7. INSERM UMR649, Centre Hospitalier Universitaire de Nantes, 44007 Nantes, France.

8. Center of Excellence for Regenerative Health Biotechnology, University of Florida, Gainesville, FL 32611.

9. Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida, Gainesville, FL 32610.

10. Powell Gene Therapy Center Vector Core, University of Florida, Gainesville, FL 32611.

11. Molecular Physiology and Therapeutics Branch, National Institute of Dental and Craniofacial Research, National Institutes of Health, Bethesda, MD 20892.

12. Laboratory of Experimental Neurosurgery, Free University of Brussels, 1070 Brussels, Belgium.

13. Multidisciplinary Research Institute, Free University of Brussels, 1070 Brussels, Belgium.

14. Center for Gene Therapy, Research Institute at Nationwide Children's Hospital, Columbus, OH 43205.

15. Department of Pediatrics, Ohio State University, Columbus, OH 43210.

16. Généthon, 91000 Evry, France.

17. Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA 01655.

18. Department of Pediatrics, University of Massachusetts Medical School, Worcester, MA 01655.

19. Molecular Medicine Laboratory, International Center for Genetic Engineering and Biotechnology (ICGEB), 34149 Trieste, Italy.

20. Infection and Cancer Program, German Cancer Research Center, 69120 Heidelberg, Germany.

21. Pharmazeutische Fabrik Dr. Reckeweg, 64625 Bensheim, Germany.

22. Division of Genetic Therapeutics, Center for Molecular Medicine, Jichi Medical University, Shimotsuke 329-0498, Japan.

23. Amsterdam Molecular Therapeutics, 1100 Amsterdam, The Netherlands.

24. Sangamo BioSciences, Richmond, CA 94804.

25. Applied Genetic Technologies, Alachua, FL 32615.

26. Center for Cellular and Molecular Therapeutics, Children's Hospital of Philadelphia, Philadelphia, PA 19104.

27. Department of Pathology and Laboratory Medicine, University of Pennsylvania School of Medicine, Philadelphia, PA 19104.

28. Department of Molecular Genetics and Microbiology, University of Florida College of Medicine, Gainesville, FL 32610.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

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