Efficacy of targeted therapy with lumacaftor/ivacaftor in children with cystic fibrosis (12-month follow-up)

Author:

Kondratieva E. I.1ORCID,Odinaeva N. D.2ORCID,Voronkova A. Yu.1,Sherman V. D.3ORCID,Zhekaite E. K.1ORCID,Orlov A. V.4,Safonova T. I.5,Kozlova E. A.6,Shulyak I. P.7,Erzutova M. V.8,Pyaterkina O. G.9,Psyurnikova O. S.10,Bondarenko T. P.11,Kondakova Yu. A.12,Seroklinov V. N.13,Ilyenkova N. A.14,Pasnova E. V.2ORCID,Fatkhullina I. R.1ORCID,Maksimycheva T. Yu.3ORCID,Kutsev S. I.3ORCID

Affiliation:

1. Research Centre for Medical Genetics named after academician N. P. Bochkov; Scientific Research Clinical Institute of Childhood Ministry of Health of the Moscow region

2. Scientific Research Clinical Institute of Childhood Ministry of Health of the Moscow region

3. Research Centre for Medical Genetics named after academician N. P. Bochkov

4. St. Olga Children’s City Hospital

5. Regional Children’s Clinical Hospital

6. Children’s Regional Clinical Hospital Ministry of Health of the Russian Federation

7. Regional Children’s Clinical Hospital No. 1

8. Volga Region Research Medical University of the Ministry of Health of Russia

9. Children’s Republican Clinical Hospital

10. Rostov region Regional Children's Clinical Hospital

11. City Ivano-Matreninskaya Children’s Clinical Hospital

12. City Children’s Clinical Hospital of Emergency Medical Care

13. Altai State Medical University

14. Krasnoyarsk State Medical University named after prof. V. F. Voino-Yasenetsky

Publisher

LLC Global Media Technology

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