Precious SMA natural history data
Author:
Publisher
Ovid Technologies (Wolters Kluwer Health)
Subject
Neurology (clinical)
Reference8 articles.
1. Infantile Muscular Atrophy
2. Darras BT , Markowitz JA , Monani UR , De Vivo DC . Spinal muscular atrophies. In: Darras BT , Jones HRJ , Ryan MM , De Vivo DC , editors. Neuromuscular Disorders of Infancy, Childhood, and Adolescence: A Clinician's Approach. San Diego: Academic Press; 2015:117–145.
3. Chaos in classification of the spinal muscular atrophies of childhood
4. Darras BT , Finkel RS . Natural history of spinal muscular atrophy. In: Sumner CJ , Paushkin S , Ko CP , editors. Spinal Muscular Atrophy: Disease Mechanisms and Therapy. San Diego: Academic Press; 2017:399–421.
5. An observational study of functional abilities in infants, children, and adults with type 1 SMA
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