Phase 1 Open-Label Study of Omigapil in Patients With LAMA2- or COL6-Related Dystrophy

Author:

Foley A. Reghan1ORCID,Yun Pomi1,Leach Meganne E.1ORCID,Neuhaus Sarah B.1,Averion Gilberto V.1ORCID,Hu Ying1ORCID,Hayes Leslie H.1ORCID,Donkervoort Sandra1ORCID,Jain Minal S.1ORCID,Waite Melissa1,Parks Rebecca1ORCID,Bharucha-Goebel Diana X.1,Mayer Oscar H.1ORCID,Zou Yaqun1ORCID,Fink Margaret1,DeCoster Jameice1,Mendoza Christopher1,Arévalo Cynthia1,Hausmann Rudolf1,Petraki Diana1,Cheung Ken1ORCID,Bönnemann Carsten G.1ORCID

Affiliation:

1. From the Neuromuscular and Neurogenetics Disorders of Childhood Section (A.R.F., P.Y., M.E.L., S.B.N., G.V.A., Y.H., L.H.H., S.D., D.X.B.-G., Y.Z., M.F., J.D., C.M., C.A., C.G.B.), Neurogenetics Branch, NINDS, NIH, Bethesda, MD; Division of Neurology (M.E.L.), Oregon Health and Science University, Portland, OR; Department of Neurology (L.H.H.), Boston Children's Hospital, MA; Rehabilitation Medicine Department (M.S.J., M.W.); Occupational Therapy Section (R.P.), Rehabilitation Medicine Department,...

Publisher

Ovid Technologies (Wolters Kluwer Health)

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