Efficacy and Safety of Elamipretide in Individuals With Primary Mitochondrial Myopathy-Reference-Cited by-同舟云学术

Efficacy and Safety of Elamipretide in Individuals With Primary Mitochondrial Myopathy

Published:2023-07-18 Issue:3 Volume:101 Page:
ISSN:0028-3878
Container-title:Neurology
language:en
Short-container-title:Neurology

Author:

Karaa Amel¹^ORCID,Bertini Enrico¹^ORCID,Carelli Valerio¹,Cohen Bruce H.¹,Enns Gregory M.¹,Falk Marni J.¹,Goldstein Amy¹,Gorman Gráinne Siobhan¹^ORCID,Haas Richard¹,Hirano Michio¹^ORCID,Klopstock Thomas¹,Koenig Mary Kay¹,Kornblum Cornelia¹,Lamperti Costanza¹,Lehman Anna¹,Longo Nicola¹,Molnar Maria Judit¹,Parikh Sumit¹,Phan Han¹,Pitceathly Robert D.S.¹^ORCID,Saneto Russell¹,Scaglia Fernando¹^ORCID,Servidei Serenella¹,Tarnopolsky Mark¹,Toscano Antonio¹,Van Hove Johan L.K.¹,Vissing John¹^ORCID,Vockley Jerry¹^ORCID,Finman Jeffrey S.¹,Brown David A.¹^ORCID,Shiffer James A.¹,Mancuso Michelango¹^ORCID,Lucia Valentino Maria,Alessandro Primiano Guido,Cristina Sancricca,Zoltan Grosz,Bathori Györgyi,Daria Diodato,Gessica Vasco,Claudia Soler-Alfonso,Ali Abdullhameed May,Michael G Hanna,Enrico Bugiardini,Olivia V Poole,Fran Kendall,A Larson,Ajantha Nithi,Kristin Engelstad,Andre Mattman,Michelle Mezei,Alamut T Bischoff,Boriana Büchner,Florentine Radelfahr,Claudia Stendel,Claudia B Catarino,Elizabeth Tonni Hilary,Tait Rossman Ian,Marie Cole Kristin,Christina Victorio Maria,Vincenzo Montano,Gabriele Siciliano,Olimpia Musumeci,Alessina Catania, ,

Affiliation:

1. From the Massachusetts General Hospital (A.K.), Harvard Medical School Boston; Neuromuscular Unit (E.B.), Bambino Gesù Ospedale Pediatrico, IRCCS, Rome; IRCCS Istituto delle Scienze Neurologiche di Bologna (V.C.), Programma di Neurogenetica; Department of Biomedical and Neuromotor Sciences (V.C.), University of Bologna, Italy; Rebecca D. Considine Research Institute (B.H.C.), Akron Children's Hospital, OH; Stanford University School of Medicine (G.M.E.), CA; Mitochondrial Medicine Frontier Program ...

Publisher

Ovid Technologies (Wolters Kluwer Health)

Subject

Neurology (clinical)

Link

https://www.neurology.org/doi/pdfdirect/10.1212/WNL.0000000000207402

Reference41 articles.

1. NORD physician guide to mitochondrial myopathies (MM);Mancuso M;Nat Org Rare Disord.,2016

2. International Workshop:

3. Mitochondrial medicine in the omics era

4. Diagnosis and treatment of mitochondrial myopathies

5. Exercise testing as a diagnostic entity in mitochondrial myopathies;Tarnopolsky M;Mitochondrion,2004

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