Enzyme Replacement Therapy: A Review and Its Role in Treating Lysosomal Storage Diseases
Author:
Publisher
SLACK, Inc.
Subject
Pediatrics, Perinatology, and Child Health
Reference30 articles.
1. Lysosomal Storage Diseases: From Pathophysiology to Therapy
2. Lysosomal storage diseases: Diagnostic confirmation and management of presymptomatic individuals
3. Emerging therapies for neuropathic lysosomal storage disorders
4. Gene therapy for lysosomal storage diseases
5. Newborn Screening for Lysosomal Storage Diseases: A Concise Review of the Literature on Screening Methods, Therapeutic Possibilities and Regional Programs
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