Perrault syndrome: The Way Forward After Genetic Counselling?

Author:

Kapil IshanORCID,Anand Rohit,Padhi Phalguni

Abstract

A female, term neonate, born via vaginal delivery to a G5P1D1A3 hypothyroid mother with a history of an elder sibling being homozygous forHSD17B4mutation, diagnosed while working up his progressive neurological disorder and succumbing to the same. The family screening revealed that both parents were heterozygous carriers of the same mutation in the geneHSD17B4. After genetic counselling, amniocentesis revealed the fetus to be having homozygosity for the same mutation. In view of precious pregnancy, normal antenatal scans and investigations, the pregnancy was continued, and baby was born with a birth weight of 2.65 kg and had a smooth perinatal transition. Parents were counselled regarding the course of the illness, possible complications and the need for regular follow-up. Ultrasound of the abdomen, pelvis and head was normal in the neonatal period. She was vaccinated as per the national schedule and gaining weight normally.

Publisher

BMJ

Reference11 articles.

1. Perrault syndrome. Available: https://rarediseases.org/rare-diseases/perrault-syndrome/ [Accessed 27 Jun 2023].

2. Deux CAS de syndrome de Turner avec Surdi-Mutité Dans une Même Fratrie [Two cases of Turner syndrome with deaf-Mutism in two sisters];Perrault;Bull Mem Soc Med Hop Paris,1951

3. Perrault syndrome: evidence for progressive nervous system involvement;Fiumara;Am J Med Genet A,2004

4. Perrault syndrome type 3 caused by diverse molecular defects in CLPP;Brodie;Sci Rep,2018

5. Perrault syndrome with neurological features in a compound heterozygote for two TWNK mutations: overlap of TWNK-related recessive disorders;Domínguez-Ruiz;J Transl Med,2019

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