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2. European Parliament, Council of the European Union. Regulation (EC) No 141/2000 of the European Parliament and of the Council of 16 December 1999 on orphan medicinal products.2000. https://eur-lex.europa.eu/legal-content/EN/TXT/PDF/?uri=CELEX:32000R0141&from=EN.
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4. Lassignardie S. Rethinking the orphan regulation. The Parliament. 2022. https://www.theparliamentmagazine.eu/news/article/rethinking-the-orphan-regulation
5. EURORDIS-Rare Diseases Europe. Breaking the access deadlock to leave no one behind. Dec 2017. https://www.eurordis.org/publications/breaking-the-access-deadlock-to-leave-no-one-behind/