What is cystic fibrosis screen positive inconclusive diagnosis? And what is it not?

Author:

Devoy EmilyORCID,Hughes DominicORCID,Alharbi Asma FalahORCID,Francis Jacqueline,Davies Jane CORCID

Abstract

Since screening for cystic fibrosis (CF) was incorporated into the newborn screening program, the number of recognised variants in theCF transmembrane conductance regulator (CFTR) gene has significantly increased. This has led to the discovery of combinations of gene variants with an uncertain prognosis. One outcome is the designation of ‘cystic fibrosis screen positive inconclusive diagnosis’ (CFSPID). While the majority of these children are expected to be unaffected by theirCFTRvariants, a small proportion have been seen to develop symptoms or increasing sweat chloride levels over time, which may reflect dysfunction of the CFTR protein.As the number of children with CFSPID increases, paediatricians and those working in primary care are more likely to encounter them in their practice. It is important that professionals have an understanding of CFSPID: what it is and, importantly, what it is not (ie, they do not have CF). In this article, we hope to explore this using some example cases, illustrating the ways in which these children may present symptomatically and how to manage them.

Publisher

BMJ

Reference10 articles.

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2. Cystic Fibrosis Screen Positive, Inconclusive Diagnosis (CFSPID): A new designation and management recommendations for infants with an inconclusive diagnosis following newborn screening

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