Review of 11 national policies for rare diseases in the context of key patient needs
Author:
Funder
Pfizer
Publisher
Springer Science and Business Media LLC
Subject
Pharmacology (medical),Genetics (clinical),General Medicine
Link
http://link.springer.com/content/pdf/10.1186/s13023-017-0618-0.pdf
Reference69 articles.
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2. Haffner ME, Whitley J, Moses M. Two decades of orphan product development. Nat Rev Drug Discov. 2002;1(10):821–5.
3. Orphan Drug Act, Public Law 97-414. 97th Congress. January 4, 1983 (US).2049-2066.
4. Orphan Drug amendments of 1985, Public Law 99, 91, 15 August 1985 (US).
5. Orphan Drug amendments of 1988, Public Law 100-290, 18 April 1988 (US).
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