1. Euoropean Commission. Pharmaceutical comittee 17 March 2015. http://ec.europa.eu/health/files/committee/74meeting/pharm684.pdf. Accessed 10 April 2015.
2. European Commission. Regulation (EC) No 141/2000 of the European parliament and of the council of 16 December 1999 on orphan medicinal products. http://ec.europa.eu/health/files/eudralex/vol-1/reg_2000_141_cons-2009-07/reg_2000_141_cons-2009-07_en.pdf. Accessed 13 Feb 2015
3. Aymé S, Rodwell C, eds. 2013 report on the state of the art of rare disease activities in Europe. 2013. http://www.eucerd.eu/upload/file/Reports/2013ReportStateofArtRDActivities.pdf. Accessed 13 Feb 2015.
4. European Commission. Policy, Rare diseases – what are they? http://ec.europa.eu/health/rare_diseases/policy/index_en.htm. Accessed 13 Feb 2015.
5. Simoens S, Picavet E, Dooms M, Cassiman D, Morel T. Cost-effectiveness assessment of orphan drugs: a scientific and political conundrum. Appl Health Econ Health Policy. 2013;11(1):1–3.