Pharmaceutical expenditure on drugs for rare diseases in Canada: a historical (2007–13) and prospective (2014–18) MIDAS sales data analysis

Author:

Divino Victoria,DeKoven Mitch,Kleinrock Michael,Wade Rolin L.,Kim Tony,Kaura Satyin

Funder

Celgene

Publisher

Springer Science and Business Media LLC

Subject

Pharmacology (medical),Genetics(clinical),General Medicine

Reference21 articles.

1. Initial draft discussion document for a Canadian orphan drug regulatory framework. Health Canada, Office of Legislative and Regulatory Modernization. 2012. http://www.orpha.net/national/data/CA-EN/www/uploads/Initial-Draft-Discussion-Document-for-A-Canadian-Orphan-Drug--Regulatory-Framework.doc . Accessed 1 Dec 2015.

2. Critchley W. Orphan drugs update – Canada. Presented at: FDLI Conference. 2014 May 14–15; Toronto, CA. http://www.fdli.org/docs/canadian/critchley-fdli-may-14-2014.pdf?sfvrsn=0 . Accessed 1 Dec 2015.

3. Lee DK, Wong B. An Orphan Drug Framework (ODF) for Canada. J Popul Ther Clin Pharmacol. 2014;21:e42–6.

4. Electronic code of federal regulations title 21 food and drugs part 316 orphan drugs. U.S. Government Publishing Office. http://www.ecfr.gov/cgi-bin/text-idx?c=ecfr&SID=238362420de6b80c19b2a9c44b73a843&rgn=div6&view=text&node=21:5.0.1.1.6.3&idno=21 . Accessed 1 Dec 2015.

5. Search orphan drug designations and approvals. U.S. Food and Drug Administration. www.accessdata.fda.gov/scripts/opdlisting/oopd/index.cfm . Accessed 28 Jul 2014.

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